We Deliver First-in-Class Therapies

We are an clinical-stage pharmaceutical company creating first-in-class therapies designed to boost expression of therapeutic genes in diseased cells.

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Close up of RNA molecule

RNAa Technology:

RNAa (RNA activation) is a platform technology to selectively turn genes on by using short duplex RNA known as small activating RNA (saRNA).

RNAa is among the limited technologies capable of stimulating the production of targeted endogenous genes.

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Our Pipeline:
The Push for the Next
Generation of Therapeutics

Ractigen has a diverse pipeline covering previously undruggable diseases and monogenic disorders including oncology, neurological and neuromuscular disorders, and liver-related indications.  

The pipeline explores the boundaries of our technology and pushes for the next generation of RNAa therapeutics.  

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Meet Our Team

Our leadership comprises a unified team of experts in RNA research and drug development, including the pioneers of RNAa technology, specialists in nucleic acid chemistry, biotech entrepreneurs, and authorities in drug discovery.

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News

09/15/2026 in Company News, Homepage News, Industry News, News Highlight

Ractigen Therapeutics to Present First-in-Human RNA Activation Data in Duchenne Muscular Dystrophy as a Late-Breaking Oral Presentation at the 31st Annual Congress of the World Muscle Society

Late-Breaking selection at the 31st Annual World Muscle Society Congress — a designation reserved for…
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08/06/2026 in Company News, Homepage News, Industry News, News Highlight, RAG-17, RAG-17 Presentation, Uncategorized

Ractigen Therapeutics Announces Completion of Enrollment and First Dosing in Phase II Clinical Trial of RAG-17 for SOD1-ALS

Nantong, China, August 6, 2026 – Ractigen Therapeutics, a clinical-stage biotechnology company pioneering next-generation RNA…
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07/31/2026 in Company News, Homepage News, Industry News, News Highlight, Uncategorized

Ractigen Therapeutics Announces U.S. FDA IND Clearance for First-in-Class saRNA Candidate RAG-1C to Treat Proliferative Vitreoretinopathy

RAG-1C achieves dual IND clearances from both U.S. FDA and China CDE, paving the way…
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07/29/2026 in Company News, Homepage News, Industry News, News Highlight, Uncategorized

Ractigen Therapeutics Closes Over $31 Million Financing to Advance Clinical-Stage saRNA Pipeline and Proprietary Extrahepatic Delivery Platforms

Funding led by Guozhong Capital will accelerate Phase 2 development for saRNA candidate RAG-01 and…
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